Tuesday, May 11, 2021

Gene Therapy Restores Immune Function in Children with Rare Immunodeficiency

The findings were published today in the New England Journal of Medicine.
NIH/NIAID Template Banner

Tuesday, May 11, 2021

Gene Therapy Restores Immune Function in Children with Rare Immunodeficiency

A DNA double helix rests on a print-out illustration of the DNA letters A, T, C and G.

An investigational gene therapy can safely restore the immune systems of infants and children who have a rare, life-threatening inherited immunodeficiency disorder, according to research supported in part by NIH. The researchers found that 48 of 50 children who received the gene therapy had retained their replenished immune system function two to three years later and did not require additional treatments for their condition, known as ADA-SCID. The findings were published today in the New England Journal of Medicine.

Read More


This email was sent to myhcistech.healthnews360@blogger.com using GovDelivery Communications Cloud on behalf of: National Institute of Allergy and Infectious Diseases · 5601 Fishers Lane · Bethesda, MD 20892 · 1-866-284-4107 GovDelivery logo

No comments:

Post a Comment